Bronstein, Gewirtz & Grossman, LLC is investigating potential claims on behalf of purchasers of Ultragenyx Pharmaceutical Inc. (“Ultragenyx” or “the Company”) (NASDAQ: RARE). Investors who purchased Ultragenyx securities are encouraged to obtain additional information and assist the investigation.

The investigation concerns whether Ultragenyx has violated federal securities laws.

Ultragenyx Investigation Details

On September 2, 2026, Ultragenyx issued a press release “announc[ing] results from the Phase 3 Aspire study for apazunersen (GTX-102) in Angelman syndrome.” Per the press release, “[t]he study did not achieve the primary endpoint of change from Baseline in Bayley-4 cognitive raw score nor the key secondary endpoint of net response in Multidomain Responder Index (MDRI).” On this news, Ultragenyx’s stock price fell $11.68 per share, or 44.03%, to close at $14.85 per share on September 3, 2026.

What’s Next for Ultragenyx Investors?

If you are aware of any facts relating to this investigation or purchased Ultragenyx securities, you can assist this investigation. You can also contact Peretz Bronstein or his client relations manager, Nathan Miller, of Bronstein, Gewirtz & Grossman, LLC: 917-590-0911